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Idursulfasa (Elaprase®) per al tractament de la mucopolisacaridosi II
(2010-01)
Background
Hunter syndrome or type II mucopolysaccharidosis (MPS II) is a lysosomal storage disease
caused by iduronate-2-sulfatase (I2S) deficiency, an enzyme involved in the metabolism of
glycoaminoglycans. It is a ...
Riociguat (Adempas®) per al tractament de la hipertensió arterial pulmonar
(2015-10)
This report aims to assess the indication for pulmonary arterial hypertension (PAH). Adempas® (riociguat) is indicated for pulmonary arterial hypertension treatment in adult patients on monotherapy or in combination with ...