Agreement between results of meta-analyses from case reports and clinical studies, regarding efficacy and safety of idursulfase therapy in patients with mucopolysaccharidosis type II (MPS-II): a new tool for evidence-based medicine in rare diseases
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Informes de casos; Estudios clínicos; Terapia de reemplazo de enzimas
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Sampayo-Cordero M, Miguel-Huguet B, Pardo-Mateos A, Malfettone A, Pérez-García J, Llombart-Cussac A, et al. Agreement between results of meta-analyses from case reports and clinical studies, regarding efficacy and safety of idursulfase therapy in patients with mucopolysaccharidosis type II (MPS-II): a new tool for evidence-based medicine in rare diseases. Orphanet J Rare Dis. 2019 Oct 21;14(1):230.
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https://hdl.handle.net/11351/5203Este elemento aparece en las siguientes colecciones
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