dc.contributor | Vall d'Hebron Barcelona Hospital Campus |
dc.contributor.author | Barrios, Kelly |
dc.contributor.author | Brown, Bob D. |
dc.contributor.author | Hoppe, Bernd |
dc.contributor.author | Rosskamp, Ralf |
dc.contributor.author | Langman, Craig B. |
dc.contributor.author | Ariceta Iraola, Gema |
dc.date.accessioned | 2021-12-16T06:44:07Z |
dc.date.available | 2021-12-16T06:44:07Z |
dc.date.issued | 2021-04 |
dc.identifier.citation | Ariceta G, Barrios K, Brown BD, Hoppe B, Rosskamp R, Langman CB. Hepatic Lactate Dehydrogenase A: An RNA Interference Target for the Treatment of All Known Types of Primary Hyperoxaluria. Kidney Int Reports. 2021 Apr;6(4):1088–98. |
dc.identifier.issn | 2468-0249 |
dc.identifier.uri | https://hdl.handle.net/11351/6691 |
dc.description | Interferencia de ARN; Lactato deshidrogenasa A; Hiperoxaluria primaria |
dc.language.iso | eng |
dc.publisher | Elsevier |
dc.relation.ispartofseries | Kidney International Reports;6(4) |
dc.rights | Attribution 4.0 International |
dc.rights.uri | http://creativecommons.org/licenses/by/4.0/ |
dc.source | Scientia |
dc.subject | Metabolisme, Errors congènits de |
dc.subject | Inhibidors enzimàtics |
dc.subject | Epigenètica |
dc.subject.mesh | Hyperoxaluria, Primary |
dc.subject.mesh | Lactate Dehydrogenases |
dc.subject.mesh | /antagonists & inhibitors |
dc.subject.mesh | RNA Interference |
dc.title | Hepatic Lactate Dehydrogenase A: An RNA Interference Target for the Treatment of All Known Types of Primary Hyperoxaluria |
dc.type | info:eu-repo/semantics/article |
dc.identifier.doi | 10.1016/j.ekir.2021.01.029 |
dc.subject.decs | hiperoxaluria primaria |
dc.subject.decs | lactato deshidrogenasas |
dc.subject.decs | /antagonistas & inhibidores |
dc.subject.decs | interferencia por ARN |
dc.relation.publishversion | https://doi.org/10.1016/j.ekir.2021.01.029 |
dc.type.version | info:eu-repo/semantics/publishedVersion |
dc.audience | Professionals |
dc.contributor.organismes | Institut Català de la Salut |
dc.contributor.authoraffiliation | [Ariceta G] Servei de Nefrologia Pediàtrica, Vall d’Hebron Hospital Universitari, Barcelona, Spain. Universitat Autònoma de Barcelona, Bellaterra, Spain. [Barrios K, Brown BD, Rosskamp R] Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA. [Hoppe B] Dicerna Pharmaceuticals, Inc., Lexington, Massachusetts, USA. German Hyperoxaluria Center Cologne/Bonn, Bonn, Germany. [Langman CB] Feinberg School of Medicine, Northwestern University, Chicago, Illinois, USA. Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, Illinois, USA |
dc.identifier.pmid | 33912759 |
dc.identifier.wos | 000639562600025 |
dc.rights.accessrights | info:eu-repo/semantics/openAccess |