| dc.contributor | Departament de Salut |
| dc.date.accessioned | 2019-04-03T08:56:08Z |
| dc.date.available | 2019-04-03T08:56:08Z |
| dc.date.issued | 2019 |
| dc.identifier.citation | Tractament de malalties minoritàries amb medicaments orfes d'autorització individual. Barcelona: Servei Català de la Salut; 2019. |
| dc.identifier.uri | https://hdl.handle.net/11351/4025 |
| dc.description | Minority diseases; Orphan drugs; Economic cost |
| dc.description.abstract | Minority diseases are a major challenge for the health system, since they often have a genetic origin, can affect many organs, be serious, represent a life threatening or being chronically debilitating. They are difficult to diagnose and have little therapeutic options; because of its characteristics require an approach multidisciplinary. |
| dc.language.iso | cat |
| dc.publisher | Servei Català de la Salut |
| dc.relation.ispartof | Programa d'harmonització farmacoterapèutica, Servei Català de la Salut |
| dc.rights | Attribution-NonCommercial-NoDerivatives 4.0 International |
| dc.rights.uri | http://creativecommons.org/licenses/by-nc-nd/4.0/ |
| dc.source | Scientia |
| dc.subject | Malalties rares - Tractament |
| dc.subject | Malalties rares - Costos |
| dc.subject | Avaluació de resultats (Assistència sanitària) |
| dc.subject.mesh | Orphan Drug Production |
| dc.subject.mesh | Outcome Assessment (Health Care) |
| dc.subject.mesh | /drug therapy |
| dc.subject.mesh | Rare Diseases |
| dc.title | Tractament de malalties minoritàries amb medicaments orfes d'autorització individual |
| dc.type | info:eu-repo/semantics/report |
| dc.subject.decs | /tratamiento farmacológico |
| dc.subject.decs | producción de medicamentos huérfanos |
| dc.subject.decs | evaluación de resultados y procesos (atención a la salud) |
| dc.subject.decs | enfermedades raras |
| dc.type.version | info:eu-repo/semantics/publishedVersion |
| dc.audience | Professionals |
| dc.rights.accessrights | info:eu-repo/semantics/openAccess |