dc.contributor | Vall d'Hebron Barcelona Hospital Campus |
dc.contributor.author | Sevilla, Julián |
dc.contributor.author | Navarro, Susana |
dc.contributor.author | Rio, Paula |
dc.contributor.author | Sánchez-Domínguez, Rebeca |
dc.contributor.author | Zubicaray, Josune |
dc.contributor.author | Galvez, Eva |
dc.contributor.author | Hladun Alvaro, Raquel |
dc.contributor.author | Díaz de Heredia Rubio, Maria Cristina |
dc.date.accessioned | 2022-02-01T12:49:19Z |
dc.date.available | 2022-02-01T12:49:19Z |
dc.date.issued | 2021-09-10 |
dc.identifier.citation | Sevilla J, Navarro S, Rio P, Sánchez-Domínguez R, Zubicaray J, Gálvez E, et al. Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes. Mol Ther Methods Clin Dev. 2021 Sep 10;22:66–75. |
dc.identifier.issn | 2329-0501 |
dc.identifier.uri | https://hdl.handle.net/11351/6945 |
dc.description | Anèmia de Fanconi; Mozobil; Teràpia gènica |
dc.description.sponsorship | This work was supported by grants from the European Commission’s Seventh Framework Program (HEALTH-F5-2012-305421 to the EUROFANCOLEN Consortium, J.A.B., J. Sevilla, C.D.-d.-H., J. Soulier, and J. Surralles), Ministerio de Sanidad, Servicios Sociales e Igualdad (EC11/060 and EC11/550 to C.D.-d.-H., J. Sevilla, J.A.B., and J. Surralles), Ministerio de Economía, Comercio y Competitividad and Fondo Europeo de Desarrollo Regional (SAF2015-68073-R, RTI2018-097125-B-I00 to P.R. and RTI2018-098419-B-I00 to J. Surralles), Fondo de Investigaciones Sanitarias at the Instituto de Salud Carlos III (RD12/0019/0023 to J.C.S.), and Consejería de Educación, Juventud y Deporte de la Comunidad de Madrid (AvanCell Project; B2017/BMD3692). CIBERER is an initiative of the Instituto de Salud Carlos III and Fondo Europeo de Desarrollo Regional. J. Surralles is supported by ICREA Academia and FARF. |
dc.language.iso | eng |
dc.publisher | Cell Press |
dc.relation.ispartofseries | Molecular Therapy. Methods & Clinical Development;22 |
dc.rights | Attribution-NonCommercial-NoDerivatives 4.0 International |
dc.rights.uri | http://creativecommons.org/licenses/by-nc-nd/4.0/ |
dc.source | Scientia |
dc.subject | Anèmia de Fanconi - Tractament |
dc.subject | Cèl·lules mare hematopoètiques - Trasplantació |
dc.subject | Teràpia cel·lular |
dc.subject.mesh | Fanconi Anemia |
dc.subject.mesh | /therapy |
dc.subject.mesh | Hematopoietic Stem Cell Transplantation |
dc.subject.mesh | /methods |
dc.title | Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes |
dc.type | info:eu-repo/semantics/article |
dc.identifier.doi | 10.1016/j.omtm.2021.06.001 |
dc.subject.decs | anemia de Fanconi |
dc.subject.decs | /terapia |
dc.subject.decs | trasplante de células madre hematopoyéticas |
dc.subject.decs | /métodos |
dc.relation.publishversion | https://doi.org/10.1016/j.omtm.2021.06.001 |
dc.type.version | info:eu-repo/semantics/publishedVersion |
dc.audience | Professionals |
dc.contributor.organismes | Institut Català de la Salut |
dc.contributor.authoraffiliation | [Sevilla J, Zubicaray J, Gálvez E] Servicio Hematología y Oncología Pediátrica, Fundación Investigación Biomédica, Hospital Infantil Universitario Niño Jesús, 28009 Madrid, Spain. Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. [Navarro S, Rio P, Sánchez-Domínguez R] Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. Hematopoietic Innovative Therapies Division, Centro de investigaciones Energéticas, Medioambientales y Tecnológicas (CIEMAT), 28040 Madrid, Spain. Instituto de Investigaciones Sanitarias Fundación Jiménez Díaz (IIS-FJD), 28040 Madrid, Spain. [Hladun R] Servei d’Oncologia Mèdica; Servei d’Hematologia Pediàtrica, Vall d’Hebron Hospital Universitari, Barcelona, Spain. Vall d’Hebron Institut de Recerca (VHIR), Barcelona, Spain. [Díaz-de-Heredia C] Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. Servei d’Oncologia Mèdica; Servei d’Hematologia Pediàtrica, Vall d’Hebron Hospital Universitari, Barcelona, Spain. Vall d’Hebron Institut de Recerca (VHIR), Barcelona, Spain |
dc.identifier.pmid | 34485595 |
dc.identifier.wos | 000695842600007 |
dc.rights.accessrights | info:eu-repo/semantics/openAccess |