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dc.contributorVall d'Hebron Barcelona Hospital Campus
dc.contributor.authorde Castro, María José
dc.contributor.authordel Toro Riera, Mireia
dc.contributor.authorGiugliani, Roberto
dc.contributor.authorCouce, Maria Luz
dc.date.accessioned2022-04-22T13:24:23Z
dc.date.available2022-04-22T13:24:23Z
dc.date.issued2021-09
dc.identifier.citationde Castro MJ, Del Toro M, Giugliani R, Couce ML. Gene Therapy for Neuronopathic Mucopolysaccharidoses: State of the Art. Int J Mol Sci. 2021 Sep;22(17):9200.
dc.identifier.issn1422-0067
dc.identifier.urihttps://hdl.handle.net/11351/7380
dc.descriptionVirus adeno associat; Lentivirus; Vectors virals
dc.description.sponsorshipThis research received no external funding.
dc.language.isoeng
dc.publisherMDPI
dc.relation.ispartofseriesInternational Journal of Molecular Sciences;22(17)
dc.rightsAttribution 4.0 International
dc.rights.urihttp://creativecommons.org/licenses/by/4.0/
dc.sourceScientia
dc.subjectMetabolisme, Errors congènits del - Tractament
dc.subjectTeràpia genètica
dc.subject.meshMucopolysaccharidoses
dc.subject.mesh/genetics
dc.subject.meshGenetic Therapy
dc.titleGene Therapy for Neuronopathic Mucopolysaccharidoses: State of the Art
dc.typeinfo:eu-repo/semantics/article
dc.identifier.doi10.3390/ijms22179200
dc.subject.decsmucopolisacaridosis
dc.subject.decs/genética
dc.subject.decsterapia genética
dc.relation.publishversionhttps://doi.org/10.3390/ijms22179200
dc.type.versioninfo:eu-repo/semantics/publishedVersion
dc.audienceProfessionals
dc.contributor.organismesInstitut Català de la Salut
dc.contributor.authoraffiliation[de Castro MJ, Couce ML] Unit of Diagnosis and Treatment of Congenital Metabolic Diseases, Department of Paediatrics, Santiago de Compostela University Clinical Hospital, 15704 Santiago de Compostela, Spain. IDIS, Health Research Institute of Santiago de Compostela, 15704 Santiago de Compostela, Spain. CIBERER, Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. MetabERN, European Reference Network for Hereditary Metabolic Disorders, 33100 Udine, Italy. [Del Toro M] CIBERER, Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. MetabERN, European Reference Network for Hereditary Metabolic Disorders, 33100 Udine, Italy. Servei de Neurologia Pediàtrica, Vall d’Hebron Hospital Universitari, Barcelona, Spain. Universitat Autònoma de Barcelona, Bellaterra, Spain. CIBERER, MetabERN, Barcelona, Spain. [Giugliani R] Medical Genetics Service, Gene Therapy Center, Medical Genetics Clinical Research Group, Biodiscovery Research Group, HCPA, Porto Alegre 90035-903, Brazil. Department of Genetics, UFRGS, Porto Alegre 91501-970, Brazil. DASA/GeneOne, São Paulo 04078-013, Brazil
dc.identifier.pmid34502108
dc.identifier.wos000694389400001
dc.rights.accessrightsinfo:eu-repo/semantics/openAccess


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