dc.contributor | Vall d'Hebron Barcelona Hospital Campus |
dc.contributor.author | de Castro, María José |
dc.contributor.author | del Toro Riera, Mireia |
dc.contributor.author | Giugliani, Roberto |
dc.contributor.author | Couce, Maria Luz |
dc.date.accessioned | 2022-04-22T13:24:23Z |
dc.date.available | 2022-04-22T13:24:23Z |
dc.date.issued | 2021-09 |
dc.identifier.citation | de Castro MJ, Del Toro M, Giugliani R, Couce ML. Gene Therapy for Neuronopathic Mucopolysaccharidoses: State of the Art. Int J Mol Sci. 2021 Sep;22(17):9200. |
dc.identifier.issn | 1422-0067 |
dc.identifier.uri | https://hdl.handle.net/11351/7380 |
dc.description | Virus adeno associat; Lentivirus; Vectors virals |
dc.description.sponsorship | This research received no external funding. |
dc.language.iso | eng |
dc.publisher | MDPI |
dc.relation.ispartofseries | International Journal of Molecular Sciences;22(17) |
dc.rights | Attribution 4.0 International |
dc.rights.uri | http://creativecommons.org/licenses/by/4.0/ |
dc.source | Scientia |
dc.subject | Metabolisme, Errors congènits del - Tractament |
dc.subject | Teràpia genètica |
dc.subject.mesh | Mucopolysaccharidoses |
dc.subject.mesh | /genetics |
dc.subject.mesh | Genetic Therapy |
dc.title | Gene Therapy for Neuronopathic Mucopolysaccharidoses: State of the Art |
dc.type | info:eu-repo/semantics/article |
dc.identifier.doi | 10.3390/ijms22179200 |
dc.subject.decs | mucopolisacaridosis |
dc.subject.decs | /genética |
dc.subject.decs | terapia genética |
dc.relation.publishversion | https://doi.org/10.3390/ijms22179200 |
dc.type.version | info:eu-repo/semantics/publishedVersion |
dc.audience | Professionals |
dc.contributor.organismes | Institut Català de la Salut |
dc.contributor.authoraffiliation | [de Castro MJ, Couce ML] Unit of Diagnosis and Treatment of Congenital Metabolic Diseases, Department of Paediatrics, Santiago de Compostela University Clinical Hospital, 15704 Santiago de Compostela, Spain. IDIS, Health Research Institute of Santiago de Compostela, 15704 Santiago de Compostela, Spain. CIBERER, Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. MetabERN, European Reference Network for Hereditary Metabolic Disorders, 33100 Udine, Italy. [Del Toro M] CIBERER, Centro de Investigación Biomédica en Red de Enfermedades Raras, 28029 Madrid, Spain. MetabERN, European Reference Network for Hereditary Metabolic Disorders, 33100 Udine, Italy. Servei de Neurologia Pediàtrica, Vall d’Hebron Hospital Universitari, Barcelona, Spain. Universitat Autònoma de Barcelona, Bellaterra, Spain. CIBERER, MetabERN, Barcelona, Spain. [Giugliani R] Medical Genetics Service, Gene Therapy Center, Medical Genetics Clinical Research Group, Biodiscovery Research Group, HCPA, Porto Alegre 90035-903, Brazil. Department of Genetics, UFRGS, Porto Alegre 91501-970, Brazil. DASA/GeneOne, São Paulo 04078-013, Brazil |
dc.identifier.pmid | 34502108 |
dc.identifier.wos | 000694389400001 |
dc.rights.accessrights | info:eu-repo/semantics/openAccess |