Browsing by Author "Perez-Garcia, Jose Manuel"
Now showing items 1-8 of 8
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Agreement between results of meta-analyses from case reports and clinical studies, regarding efficacy and safety of idursulfase therapy in patients with mucopolysaccharidosis type II (MPS-II): a new tool for evidence-based medicine in rare diseases
Miguel-Huguet, Bernat; Pardo-Mateos, Almudena; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Moltó Abad, Marc Miquel; Pérez López, Jorge; Sampayo-Cordero, Miguel; Malfettone, Andrea (Springer Nature, 2019-10-21) -
CDK4/6 Inhibitors in Hormone Receptor-Positive Metastatic Breast Cancer: Current Practice and Knowledge
de Melo Gagliato, Debora; Buzaid, Antonio C; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Cortés Castan, Javier (MDPI, 2020-09-01) -
Inclusion of non-inferiority analysis in superiority-based clinical trials with single-arm, two-stage Simon's design
Miguel-Huguet, Bernat; Perez-Garcia, Jose Manuel; Páez, David; Guerrero‑Zotano, Angel; Garde-Noguera, Javier; Cortés Castan, Javier; Sampayo-Cordero, Miguel (Elsevier, 2020-11-01) -
Molecular Features of Metaplastic Breast Carcinoma: An Infrequent Subtype of Triple Negative Breast Carcinoma
González-Martínez, Silvia; Pérez-Mies, Belén; Carretero-Barrio, Irene; Palacios-Berraquero, María Luisa; Perez-Garcia, Jose Manuel; Cortés Castan, Javier (MDPI, 2020-07-08) -
Surrogate endpoints for early-stage breast cancer: a review of the state of the art, controversies, and future prospects
Gion, María; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Cortés Castan, Javier; Sampayo-Cordero, Miguel; Malfettone, Andrea (SAGE Publications, 2021-01-01) -
The Impact of Excluding Nonrandomized Studies From Systematic Reviews in Rare Diseases: “The Example of Meta-Analyses Evaluating the Efficacy and Safety of Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis”
Miguel-Huguet, Bernat; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Cortés Castan, Javier; Pérez López, Jorge; Sampayo-Cordero, Miguel; Malfettone, Andrea (Frontiers Media, 2021-06-22) -
The Value of Case Reports in Systematic Reviews from Rare Diseases. The Example of Enzyme Replacement Therapy (ERT) in Patients with Mucopolysaccharidosis Type II (MPS-II)
Miguel-Huguet, Bernat; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Cortés Castan, Javier; Pérez López, Jorge; Sampayo-Cordero, Miguel; Malfettone, Andrea (MDPI, 2020-09-10) -
Trastuzumab Emtansine Plus Non-Pegylated Liposomal Doxorubicin in HER2-Positive Metastatic Breast Cancer (Thelma): A Single-Arm, Multicenter, Phase Ib Trial
López-Miranda, Elena; Perez-Garcia, Jose Manuel; Brain, Etienne; Ravnik, Maja; Escriva de Romaní Muñoz, Santiago Ignacio; Cortés Castan, Javier; Di Cosimo, Serena (MDPI, 2020-11-25)