Browsing by Author "Miguel-Huguet, Bernat"
Now showing items 1-5 of 5
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A single-arm study design with non-inferiority and superiority time-to-event endpoints: a tool for proof-of-concept and de-intensification strategies in breast cancer
Sampayo-Cordero, Miguel; Miguel-Huguet, Bernat; Malfettone, Andrea; López-Miranda, Elena; Gion, María; Abad, Elena; Cortes, Javier (Frontiers Media, 2023-07-11) -
Agreement between results of meta-analyses from case reports and clinical studies, regarding efficacy and safety of idursulfase therapy in patients with mucopolysaccharidosis type II (MPS-II): a new tool for evidence-based medicine in rare diseases
Miguel-Huguet, Bernat; Pardo-Mateos, Almudena; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Moltó Abad, Marc Miquel; Pérez López, Jorge; Sampayo-Cordero, Miguel; Malfettone, Andrea (Springer Nature, 2019-10-21) -
Inclusion of non-inferiority analysis in superiority-based clinical trials with single-arm, two-stage Simon's design
Miguel-Huguet, Bernat; Perez-Garcia, Jose Manuel; Páez, David; Guerrero‑Zotano, Angel; Garde-Noguera, Javier; Cortés Castan, Javier; Sampayo-Cordero, Miguel (Elsevier, 2020-11-01) -
The Impact of Excluding Nonrandomized Studies From Systematic Reviews in Rare Diseases: “The Example of Meta-Analyses Evaluating the Efficacy and Safety of Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis”
Miguel-Huguet, Bernat; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Cortés Castan, Javier; Pérez López, Jorge; Sampayo-Cordero, Miguel; Malfettone, Andrea (Frontiers Media, 2021-06-22) -
The Value of Case Reports in Systematic Reviews from Rare Diseases. The Example of Enzyme Replacement Therapy (ERT) in Patients with Mucopolysaccharidosis Type II (MPS-II)
Miguel-Huguet, Bernat; Perez-Garcia, Jose Manuel; Llombart-Cussac, Antonio; Cortés Castan, Javier; Pérez López, Jorge; Sampayo-Cordero, Miguel; Malfettone, Andrea (MDPI, 2020-09-10)